Penyakit yang berpotensi dapat diterapi dengan Sel Punca

Leukemia Akut

Acute Biphenotypic Leukaemia. Acute Lymphocytic Leukaemia (ALL). Acute Myelogenous Leukaemia (AML). Acute Lymphoblastic Leukaemia. Acute Undifferentiated Leukaemia

Leukemia Kronik

Chronic Lymphocytic Leukaemia (CLL). Chronic Myelogenous Leukaemia (CML). Juvenile Chronic Myelogenous Leukaemia (JCML). Juvenile Myelomonocytic Leukaemia (JMML). Juvenile Myelogenous Leukaemia

Sindrom Myelodysplastic

Amyloidosis. Chronic Myelomonocytic Leukaemia (CMML). Refractory Anaemia (RA). Refractory Anaemia with Excess Blasts (RAEB). Refractory Anaemia with Excess Blasts in Transformation (RAEB-T). Refractory Anaemia with Ringed Sideroblasts (RARS)

Myeloproliferative Disorders 

Acute Myelofibrosis. Agnogenic Myeloid Metaplasia (Myelofibrosis). Essential Thrombocythemia. Polycythemia Vera

Lymphoproliferative Disorders

Hodgkin’s Disease. Non-Hodgkin’s Lymphoma. Prolymphocytic Leukaemia

Kelainan Genetik pada Metabolisme

Adrenoleukodystrophy. Alpha Mannosidosis. Beta-Glucuronidase Deficiency (MPS-Vll). Gaucher’s Disease. Hunter’s Syndrome (MPS-ll). Hurler’s Syndrome (MPS-lH). Krabbe Disease. Maroteaux-Lamy Syndrome (MPS-Vl). Metachromatic Leukodystrophy. Morquio Syndrome (MPS-lV). Mucolipidosis II (l-cell Disease). Mucopolysaccharidoses (MPS). Niemann-Pick Disease. Sanfilippo Syndrome (MPS-lll). Scheie Syndrome (MPS-lS). Sly Syndrome. Wolman Disease

Kelainan Genetik Sel Trombosit

Amegakaryocytosis / Congenital Thrombocytopenia

Abnormalitas Genetik Sel Eritrosit

Beta Thalassaemia Major. Blackfan-Diamond Anaemia. Pure Red Cell Aplasia. Sickle Cell Disease

Kelainan Sistem Fagosit

Chediak-Higashi Syndrome. Chronic Granulomatous Disease. Neutrophil Actin Deficiency. Reticular Dysgenesis

Kelainan Histiositik

Familial Eritrofagosit. Limfohistiositosis. Hemofagositosis. Histiositosis-X. Histiositosis Sel Langerhans

Kelainan Genetik Kongenital Sistem Kekebalan Tubuh

Absence of T & B Cells SCID. Absence of T Cells, Normal B Cell SCID. Ataxia-Telangiectasia. Bare Lymphocyte Syndrome. Common Variable Immunodeficiency. DiGeorge Syndrome. Kostmann Syndrome. Leukocyte Adhesion Deficiency. Omenn’s Syndrome. Severe Combined Immunodeficiency (SCID). SCID with Adenosine Deaminase. Deficiency. Wiskott-Aldrich Syndrome. X-Linked Lymphoproliferative Disorder

Kelainan Sel Punca

Aplastic Anaemia (Severe). Congenital Cytopenia. Dyskeratosis Congenita. Fanconi Anaemia.

Kelainan Sel Plasma

Multiple Myeloma. Plasma Cell Leukaemia. Waldenstrom’s Macroglobulinemia

Kelainan Genetik Lainnya

Cartilage-Hair Hypoplasia. Ceroid Lipofuscinosis. Congenital Erythropoietic Porphyria. Glanzmann Thrombasthenia Lesch-Nyhan Syndrome. Osteopetrosis. Tay Sachs Disease

Terapi Yang Masih Dalam Tahap Pengembangan

Diabetes. Cerebral Palsy. Cedera Otak. Penyakit Jantung. Stroke